{"id":26559,"date":"2026-01-27T23:19:21","date_gmt":"2026-01-27T14:19:21","guid":{"rendered":"http:\/\/mhjn.dothome.co.kr\/%ec%8a%a4%ec%b9%b4%ec%9d%b4%ed%98%b8%ed%81%ac-%ed%85%8c%eb%9d%bc%ed%93%a8%ed%8b%b1%ec%8a%a4-%ed%97%8c%ed%8c%85%ed%84%b4%eb%b3%91-%ec%b9%98%eb%a3%8c%ec%a0%9c-sky-0515-%ec%a0%9c1%ec%83%81-%ec%9e%84\/"},"modified":"2026-08-20T11:14:37","modified_gmt":"2026-08-20T11:14:37","slug":"%ec%8a%a4%ec%b9%b4%ec%9d%b4%ed%98%b8%ed%81%ac-%ed%85%8c%eb%9d%bc%ed%93%a8%ed%8b%b1%ec%8a%a4-%ed%97%8c%ed%8c%85%ed%84%b4%eb%b3%91-%ec%b9%98%eb%a3%8c%ec%a0%9c-sky-0515-%ec%a0%9c1%ec%83%81-%ec%9e%84","status":"publish","type":"post","link":"http:\/\/mhjn.dothome.co.kr\/en\/%ec%8a%a4%ec%b9%b4%ec%9d%b4%ed%98%b8%ed%81%ac-%ed%85%8c%eb%9d%bc%ed%93%a8%ed%8b%b1%ec%8a%a4-%ed%97%8c%ed%8c%85%ed%84%b4%eb%b3%91-%ec%b9%98%eb%a3%8c%ec%a0%9c-sky-0515-%ec%a0%9c1%ec%83%81-%ec%9e%84\/","title":{"rendered":"\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4, \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc\uc81c SKY-0515 \uc81c1\uc0c1 \uc784\uc0c1\uc2dc\ud5d8 \ud658\uc790 \ub300\uc0c1 9\uac1c\uc6d4 \uc911\uac04 \uacb0\uacfc \ubc1c\ud45c"},"content":{"rendered":"<p><img decoding=\"async\" src=\"http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/01\/Skyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg\" title=\"\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4, \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc\uc81c SKY-0515 \uc81c1\uc0c1 \uc784\uc0c1\uc2dc\ud5d8 \ud658\uc790 \ub300\uc0c1 9\uac1c\uc6d4 \uc911\uac04 \uacb0\uacfc \ubc1c\ud45c\" \/><\/p>\n<table border=\"0\" cellspacing=\"10\" cellpadding=\"5\" align=\"right\">\n<tbody>\n<tr>\n<td><img decoding=\"async\" src=\"http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/01\/Skyhawk_Therapeutics_Logo.jpg\" border=\"0\" alt=\"\" title=\"logo\" hspace=\"0\" vspace=\"0\" width=\"118\" \/><\/td>\n<\/tr>\n<\/tbody>\n<\/table>\n<p class=\"prntac\"><i>9\uac1c\uc6d4 \ubd84\uc11d \uacb0\uacfc \ubcf5\ud569 \ud1b5\ud569 \ud5cc\ud305\ud134\ubcd1 \ub4f1\uae09 \ucc99\ub3c4\uac00 \uae30\uc800\uce58 \ub300\ube44 \ud3c9\uade0 0.64\uc810 \uac1c\uc120-\uc131\ud5a5 \uc810\uc218 \uac00\uc911\uce58 \uc801\uc6a9 \uc2dc \uc99d\uc0c1 \ubc1c\ud604 \ud658\uc790\uc758 9\uac1c\uc6d4 \uc608\uc0c1 \uc790\uc5f0 \uacbd\uacfc \uc545\ud654 \uc218\uce58\uc778 -0.73\uc810 \ub300\ube44<\/i><\/p>\n<p class=\"prntac\"><i>\uc2a4\uce74\uc774\ud638\ud06c, SKY-0515\uc758 \uc784\uc0c1 2\/3\uc0c1\uc778 FALCON-HD \uc2dc\ud5d8\uc744 \uc804 \uc138\uacc4\ub85c \ud655\ub300\ud55c\ub2e4\uace0 \ubc1c\ud45c- \ud604\uc7ac\uae4c\uc9c0 90\uba85 \uc774\uc0c1\uc758 \ud658\uc790\uc5d0\uac8c \ud22c\uc57d \uc2dc\ud589<\/i><\/p>\n<p><span class=\"legendSpanClass\">\ubcf4\uc2a4\ud134<\/span>, <span class=\"legendSpanClass\">2026\ub144 1\uc6d4 27\uc77c<\/span> \/PRNewswire\/ &#8212; \uc911\uc694\ud55c RNA \ud45c\uc801\uc744 \uc870\uc808\ud558\ub294 \ud601\uc2e0\uc801 \uc800\ubd84\uc790 \uce58\ub8cc\uc81c\ub97c \uac1c\ubc1c \uc911\uc778 \uc784\uc0c1 \ub2e8\uacc4 \ubc14\uc774\uc624\ud14c\ud06c \uae30\uc5c5 <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=1326970215&amp;u=https%3A%2F%2Fedge.prnewswire.com%2Fc%2Flink%2F%3Ft%3D0%26l%3Den%26o%3D4603860-1%26h%3D3220405556%26u%3Dhttps%253A%252F%252Fwww.skyhawktx.com%252F%26a%3DSkyhawk%2BTherapeutics%252C%2BInc.&amp;a=%EC%8A%A4%EC%B9%B4%EC%9D%B4%ED%98%B8%ED%81%AC+%ED%85%8C%EB%9D%BC%ED%93%A8%ED%8B%B1%EC%8A%A4(Skyhawk+Therapeutics%2C+Inc.)\" target=\"_blank\" rel=\"nofollow\">\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4(Skyhawk Therapeutics, Inc.)<\/a>\uac00 1\uc6d4 27\uc77c \uc790\uc0ac\uc758 \ud5cc\ud305\ud134\ubcd1(Huntington&#8217;s disease, HD) \uc784\uc0c1\uc2dc\ud5d8 \uce58\ub8cc\uc81c\uc778 SKY-0515\uc758 9\uac1c\uc6d4 \uc911\uac04 \ubd84\uc11d\uc5d0\uc11c \uae0d\uc815\uc801\uc778 \uacb0\uacfc\uac00 \ub3c4\ucd9c\ub410\ub2e4\uace0 \ubc1c\ud45c\ud588\ub2e4.<\/p>\n<div dir=\"ltr\">   <a href=\"http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/01\/Skyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg\" target=\"_blank\"><img decoding=\"async\" title=\"Skyhawk Therapeutics, Inc.\" src=\"http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/01\/Skyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg\" alt=\"Skyhawk Therapeutics, Inc.\" align=\"middle\" \/><\/a>   <br \/>   <span>Skyhawk Therapeutics, Inc.<\/span>  <\/div>\n<p>SKY-0515 \ud22c\uc5ec \uacb0\uacfc 9mg \uc6a9\ub7c9\uc5d0\uc11c \ud608\uc561 \ub0b4 \ubcc0\uc774 \ud5cc\ud305\ud2f4 \ub2e8\ubc31\uc9c8(mHTT)\uc774 62% \uac10\uc18c\ud558\ub294 \ub4f1 \uc6a9\ub7c9 \uc758\uc874\uc801 \uac10\uc18c\uac00 \ub098\ud0c0\ub0ac\uc73c\uba70, \uccb4\uc138\ud3ec CAG \ubc18\ubcf5 \ud655\uc7a5 \ubc0f \ud5cc\ud305\ud134\ubcd1 \ubcd1\ub9ac\ud559\uc758 \ud575\uc2ec \ub3d9\uc778\uc778 PMS1 mRNA\ub294 26% \uac10\uc18c\ud588\ub2e4. \ub610\ud55c SKY-0515\ub294 \uc6b0\uc218\ud55c \uc911\ucd94\uc2e0\uacbd\uacc4 \ub178\ucd9c\uc744 \uc785\uc99d\ud588\uc73c\uba70 \uc804\ubc18\uc801\uc73c\ub85c \uc548\uc804\ud558\uace0 \ub0b4\uc57d\uc131\uc774 \uc6b0\uc218\ud55c \uac83\uc73c\ub85c \ub098\ud0c0\ub0ac\ub2e4.<\/p>\n<p>\uc81c1\uc0c1 \uc784\uc0c1\uc2dc\ud5d8 \ud30c\ud2b8 C \ud658\uc790 \ucf54\ud638\ud2b8\uc5d0\uc11c SKY-0515\ub97c \ud22c\uc5ec\ubc1b\uc740 \ud658\uc790\ub4e4\uc740 3\uac1c\uc6d4, 6\uac1c\uc6d4, 9\uac1c\uc6d4 \ucc28\uc5d0 \uae30\uc800\uce58 \ub300\ube44 \ud3c9\uade0 \ubcf5\ud569 \ud1b5\ud569 \ud5cc\ud305\ud134\ubcd1 \ub4f1\uae09 \ucc99\ub3c4(Composite Unified Huntington&#8217;s Disease Rating Scale, cUHDRS)\uc758 \uac1c\uc120\uc744 \ubcf4\uc600\ub2e4. 9\uac1c\uc6d4 \ucc28 \ud1b5\ud569 \ubd84\uc11d\uc5d0\uc11c \ud655\uc778\ub41c \uac1c\uc120 \uc218\uce58\ub294 +0.64\uc810\uc73c\ub85c, \uc774\ub294 Enroll-HD \ubc0f TRACK-HD\ub97c \ud65c\uc6a9\ud55c \uc131\ud5a5 \uc810\uc218 \uac00\uc911\uce58 \uae30\uc900 \uc99d\uc0c1 \ubc1c\ud604 \ud658\uc790\uc758 9\uac1c\uc6d4 \uc608\uc0c1 \uc545\ud654 \uc218\uce58\uc778 -0.73\uc810\uacfc \ube44\uad50\ub418\ub294 \uc218\uce58\ub2e4.<\/p>\n<p>\uc720\ub2c8\ubc84\uc2dc\ud2f0 \uce7c\ub9ac\uc9c0 \ub7f0\ub358\uc758 \uc5d0\ub4dc \uc640\uc77c\ub4dc(Ed Wild) \uc2e0\uacbd\ud559 \uad50\uc218\ub294 &#8220;\ud658\uc790 \ub300\uc0c1 SKY-0515 \uc784\uc0c1 1\uc0c1 \ud30c\ud2b8 C\uc5d0\uc11c \ud655\uc778\ub41c \uc548\uc804\uc131 \ubc0f \ucd08\uae30 \ud6a8\ub2a5 \ub370\uc774\ud130\uc5d0 \ub9e4\uc6b0 \uace0\ubb34\ub3fc \uc788\uc73c\uba70, \ud2b9\ud788 \uc0ac\uc804 \uc124\uc815\ub41c 3, 6, 9\uac1c\uc6d4 \ubd84\uc11d\uc5d0\uc11c cUHDRS \uc218\uce58\uac00 \uc608\uc0c1\ub418\ub294 \uc790\uc5f0 \uacbd\uacfc\uc801 \uc545\ud654 \uc591\uc0c1\uc5d0\uc11c \ubc97\uc5b4\ub098\ub294 \uac83\uc744 \ud655\uc778\ud588\ub2e4&#8221;\ub77c\uace0 \ubc1d\ud614\ub2e4. \ub610\ud55c &#8220;SKY-0515\ub294 \ud604\uc7ac\uae4c\uc9c0 \ud658\uc790\ub97c \ub300\uc0c1\uc73c\ub85c \ud14c\uc2a4\ud2b8\ub41c \uadf8 \uc5b4\ub5a4 \uce58\ub8cc\uc81c\ubcf4\ub2e4 \ud070 \ud3ed\uc73c\ub85c mHTT \ub2e8\ubc31\uc9c8\uc744 \uc9c0\uc18d\uc801\uc73c\ub85c \uac10\uc18c\uc2dc\ud0a4\uace0 \uc788\uc73c\uba70, \uc784\uc0c1 \ubc0f \uc0dd\uccb4 \ud45c\uc9c0\uc790\uc0dd\uccb4\ud45c\uc9c0\uc790 \ub370\uc774\ud130\ub294 \uc774 \uc57d\ubb3c\uc774 \ud14c\uc2a4\ud2b8\ub41c \ubaa8\ub4e0 \uc6a9\ub7c9\uc5d0\uc11c \ub0b4\uc57d\uc131\uc774 \uc6b0\uc218\ud568\uc744 \ubcf4\uc5ec\uc900\ub2e4. mHTT\uc640 PMS1\uc744 \ubaa8\ub450 \uac10\uc18c\uc2dc\ud0a4\ub294 SKY-0515\uc758 \ub2a5\ub825\uc740 \ub450 \uac00\uc9c0 \ud575\uc2ec \ubcd1\uc6d0\uc131 \uae30\uc804\uc744 \ud1b5\ud574 \ud5cc\ud305\ud134\ubcd1\uc744 \uce58\ub8cc\ud560 \uc218 \uc788\ub294 \uac15\ub825\ud55c \uc870\ud569\uc744 \uc81c\uacf5\ud55c\ub2e4. \ud604\uc7ac \uc9c4\ud589 \uc911\uc778 \uc704\uc57d \ub300\uc870 FALCON-HD \uc2dc\ud5d8\uc5d0\uc11c \uac80\uc99d\ub420 \uc774\ubc88 \uacf5\uac1c \uc2dc\ud5d8 \uacb0\uacfc\ub294 \uc804 \uc138\uacc4 \ud5cc\ud305\ud134\ubcd1 \ud658\uc790\ub4e4\uc5d0\uac8c \uc720\uc758\ubbf8\ud55c \uc601\ud5a5\uc5d0 \ub300\ud55c \uae30\ub300\ub97c \uc2ec\uc5b4\uc8fc\uba70, SKY-0515\uc640 \uac19\uc740 \uacbd\uad6c\uc6a9 \ud5cc\ud305\ud2f4 \uac10\uc18c \uce58\ub8cc\uc81c\ub294 \uc9c4\uc815\uc73c\ub85c \ud601\uc2e0\uc801\uc778 \ubcc0\ud654\ub97c \uac00\uc838\uc62c \uac83\uc774\ub2e4&#8221;\ub77c\uace0 \ub367\ubd99\uc600\ub2e4.<\/p>\n<p>\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4\uc758 \uc138\ub974\uac8c\uc774 \ud30c\uc6b0\uc2dc\ud0a8(Sergey Paushkin) \uc5f0\uad6c\uac1c\ubc1c \ucd1d\uad04\uc740 &#8220;\ub2f9\uc0ac \uc81c1\uc0c1 \uc2dc\ud5d8\uc758 \ubaa9\ud45c\ub294 \uc548\uc804\uc131\uacfc \uc0dd\uccb4 \ud45c\uc9c0\uc790 \ud65c\uc131\uc744 \ud655\ub9bd\ud558\ub294 \uac83\uc774\uc5c8\ub2e4&#8221;\ub77c\uba70 &#8220;9\uac1c\uc6d4 \uc911\uac04 \ub370\uc774\ud130 \ubd84\uc11d\uc5d0\uc11c \ub098\ud0c0\ub09c SKY-0515\uc758 \uac15\ub825\ud55c \uc0dd\uccb4 \ud45c\uc9c0\uc790 \ubc18\uc751\uacfc \uc790\uc5f0\uacbd\uacfc \ub370\uc774\ud130 \ub300\ube44 cUHDRS\uc758 \uac1c\uc120 \uacb0\uacfc\ub294 SKY-0515\uac00 \ud5cc\ud305\ud134\ubcd1\uc5d0 \ub300\ud55c \ubca0\uc2a4\ud2b8 \uc778 \ud074\ub798\uc2a4(best in class) \uc9c8\ud658 \uc870\uc808 \uce58\ub8cc\uc81c\uac00 \ub420 \uc7a0\uc7ac\ub825\uc744 \uac15\uc870\ud55c\ub2e4. \uc774\ubc88 \uc911\uac04 \ub370\uc774\ud130\ub294 SKY-0515\uc758 \uc911\uc694\ud55c \uc774\uc815\ud45c\uc774\uba70, \uc2b9\uc778\ub41c \uc9c8\ud658 \uc870\uc808 \uce58\ub8cc\uc81c\uac00 \uc5c6\ub294 \uce58\uba85\uc801\uc778 \uc9c8\ud658\uc5d0 \ub300\ud574 \uc800\ubd84\uc790 \ud654\ud569\ubb3c \uc2e0\uc57d\ubb3c\uc9c8(first-in-class)\uc744 \uc81c\uacf5\ud558\ub294 \uc2a4\uce74\uc774\ud638\ud06c \ud50c\ub7ab\ud3fc\uc758 \uc704\ub825\uc744 \ubcf4\uc5ec\uc8fc\ub294 \uac83\uc774\ub2e4&#8221;\ub77c\uace0 \ub9d0\ud588\ub2e4.<\/p>\n<p>\ud5cc\ud305\ud134\ubcd1\uc740 \ud76c\uadc0\ud558\uace0 \uc720\uc804\uc801\uc774\uba70 \uacb0\uad6d \uce58\uba85\uc801\uc778 \uacb0\uacfc\ub97c \ucd08\ub798\ud558\ub294 \uc2e0\uacbd\ud1f4\ud589\uc131 \uc9c8\ud658\uc73c\ub85c, \ubbf8\uad6d \ub0b4 4\ub9cc \uba85 \uc774\uc0c1\uc758 \uc99d\uc0c1 \ubc1c\ud604 \ud658\uc790\uac00 \uc788\uc73c\uba70 \uc804 \uc138\uacc4\uc801\uc73c\ub85c \uc218\uc2ed\ub9cc \uba85\uc774 \uc774\ub97c \uc553\uace0 \uc788\ub294 \uac83\uc73c\ub85c \ucd94\uc815\ub41c\ub2e4. \ud604\uc7ac \uc9c8\ubcd1\uc758 \uc9c4\ud589\uc744 \ub2a6\ucd94\uac70\ub098 \uba48\ucd94\ub294 \uc2b9\uc778\ub41c \uce58\ub8cc\uc81c\ub294 \uc5c6\ub2e4. SKY-0515\ub294 \ud68c\uc0ac\uc758 \ud601\uc2e0\uc801\uc778 RNA \uc870\uc808 \ud50c\ub7ab\ud3fc\uc778 SKYSTAR\u00ae\ub97c \ud1b5\ud574 \uac1c\ubc1c\ub41c \uacbd\uad6c\uc6a9 \uc870\uc0ac\uc6a9 \uc800\ubd84\uc790 RNA \uc870\uc808\uc81c\ub2e4. SKY-0515\ub294 HTT \ub2e8\ubc31\uc9c8\uacfc PMS1 \ub2e8\ubc31\uc9c8\uc744 <i>\ubaa8\ub450<\/i> \uce58\ub8cc\uc801\uc73c\ub85c \uac10\uc18c\uc2dc\ud0a8\ub2e4. PMS1\uc740 \uccb4\uc138\ud3ec CAG \ubc18\ubcf5 \ud655\uc7a5 \ubc0f \ud5cc\ud305\ud134\ubcd1 \ubcd1\ub9ac\ud559\uc758 \ub610 \ub2e4\ub978 \ud575\uc2ec \ub3d9\uc778\uc73c\ub85c, \ubcc0\uc774 HTT \uac10\uc18c\uc758 \uc774\uc810\uc744 \ubcf4\uc644\ud560 \uac83\uc73c\ub85c \uae30\ub300\ub41c\ub2e4.<\/p>\n<p>\uc2a4\uce74\uc774\ud638\ud06c\ub294 \ub610\ud55c \ud638\uc8fc\uc640 \ub274\uc9c8\ub79c\ub4dc \ub0b4 12\uac1c \uae30\uad00\uc5d0\uc11c \uc9c4\ud589 \uc911\uc778 SKY-0515 \uc81c 2\/3\uc0c1 FALCON-HD \uc2dc\ud5d8\uc744 \uc804 \uc138\uacc4\ub85c \ud655\ub300\ud588\ub2e4\uace0 \ubc1c\ud45c\ud588\ub2e4. \uc2a4\uce74\uc774\ud638\ud06c\ub294 \ud604\uc7ac\uae4c\uc9c0 90\uba85 \uc774\uc0c1\uc758 \ud658\uc790\uc5d0\uac8c SKY-0515 \ud22c\uc57d\uc744 \uc644\ub8cc\ud588\ub2e4.<\/p>\n<p>SKY-0515\ub294 \uc2a4\uce74\uc774\ud638\ud06c\uac00 \ucc98\uc74c\uc73c\ub85c \uc784\uc0c1 \uc2dc\ud5d8\uc744 \uc9c4\ud589\ud55c \uc57d\ubb3c\uc774\ub2e4.<\/p>\n<p>\uc2a4\uce74\uc774\ud638\ud06c\ub294 2027\ub144 \ub9d0\uae4c\uc9c0 \uc2b9\uc778\ub41c \uc9c8\ud658 \uc870\uc808 \uce58\ub8cc\uc81c\uac00 \uc5c6\ub294 \ud76c\uadc0 \uc2e0\uacbd\uacc4 \uc9c8\ud658 \uce58\ub8cc\ub97c \uc704\ud55c \ucd94\uac00 \uc800\ubd84\uc790 \uc57d\ubb3c\ub4e4\uc744 \uc784\uc0c1 \ub2e8\uacc4\uc5d0 \uc9c4\uc785\uc2dc\ud0ac \uacc4\ud68d\uc774\ub2e4.<\/p>\n<p><b>SKY-0515 \uc81c1\uc0c1 \uc784\uc0c1\uc2dc\ud5d8 \uc18c\uac1c<\/b><\/p>\n<p>SKY-0515 \uc81c1\uc0c1 \uc784\uc0c1\uc2dc\ud5d8\uc740 \uac74\uac15\ud55c \uc9c0\uc6d0\uc790\uc640 \ucd08\uae30 \ub2e8\uacc4 \ud5cc\ud305\ud134\ubcd1 \ud658\uc790\ub97c \ub300\uc0c1\uc73c\ub85c SKY-0515\uc758 \uc548\uc804\uc131, \ub0b4\uc57d\uc131, \uc57d\ub3d9\ud559 \ubc0f \uc57d\ub825\ud559\uc744 \ud3c9\uac00\ud558\uae30 \uc704\ud55c \ucd5c\ucd08\uc758 \uc778\uac04 \ub300\uc0c1 \uc784\uc0c1\uc2dc\ud5d8\uc774\ub2e4. \uc2dc\ud5d8\uc740 \uc138 \ud30c\ud2b8\ub85c \ub098\ub25c\ub2e4. \ud30c\ud2b8 A\uc640 B\ub294 \uac74\uac15\ud55c \uc9c0\uc6d0\uc790\ub97c \ub300\uc0c1\uc73c\ub85c SKY-0515\ub97c \ud3c9\uac00\ud588\ub2e4. \ud30c\ud2b8 C\ub294 \ucd08\uae30 \ub2e8\uacc4 \ud5cc\ud305\ud134\ubcd1 \ud658\uc790(HD-ISS 1, 2\ub2e8\uacc4 \ub610\ub294 \uacbd\ubbf8\ud55c 3\ub2e8\uacc4)\ub97c \ub300\uc0c1\uc73c\ub85c \ub450 \uac00\uc9c0 \uc6a9\ub7c9 \uc218\uc900\uc758 SKY-0515\uc640 \uc704\uc57d\uc744 84\uc77c\uac04 \ud22c\uc5ec\ud558\ub294 \uc774\uc911\ub208\uac00\ub9bc, \uc704\uc57d \ub300\uc870, \ubcd1\ub82c \uc124\uacc4 \uc2dc\ud5d8\uc73c\ub85c, \ubaa8\ub4e0 \ucc38\uac00\uc790\ub294 12\uac1c\uc6d4\uc758 \ud65c\uc131 \ud22c\uc5ec \uc5f0\uc7a5 \uae30\uac04 \ub3d9\uc548 \ub208\uac00\ub9bc \ubc29\uc2dd\uc73c\ub85c \uc800\uc6a9\ub7c9 \ub610\ub294 \uace0\uc6a9\ub7c9\uc758 SKY-0515\ub97c \ud22c\uc5ec\ubc1b\ub294\ub2e4. \uc2dc\ud5d8 \ubaa9\uc801\uc5d0\ub294 \ubcc0\uc774 HTT \ub2e8\ubc31\uc9c8 \ubc0f PMS1 mRNA \ud3c9\uac00\uac00 \ud3ec\ud568\ub41c\ub2e4. SKY-0515 \ud30c\ud2b8 C\uc758 \uccab \ud658\uc790 \ud22c\uc57d\uc740 2025\ub144 1\uc6d4\uc5d0 \uc2dc\uc791\ub410\uc73c\uba70, \ud604\uc7ac \uc81c1C\uc0c1 \ub2e8\uacc4\uc758 \ub4f1\ub85d\uc774 \uc644\ub8cc\ub410\ub2e4.<\/p>\n<p><b>SKY-0515 \uc81c2\/3\uc0c1 FALCON-HD \uc784\uc0c1\uc2dc\ud5d8 \uc18c\uac1c<\/b><\/p>\n<p><b>FALCON-HD<\/b>(<a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=3584404727&amp;u=https%3A%2F%2Fedge.prnewswire.com%2Fc%2Flink%2F%3Ft%3D0%26l%3Den%26o%3D4603860-1%26h%3D1632102172%26u%3Dhttps%253A%252F%252Fc212.net%252Fc%252Flink%252F%253Ft%253D0%2526l%253Den%2526o%253D4450835-1%2526h%253D1917935461%2526u%253Dhttps%25253A%25252F%25252Fclinicaltrials.gov%25252Fstudy%25252FNCT06873334%2526a%253DNCT06873334%26a%3DNCT06873334&amp;a=NCT06873334\" target=\"_blank\" rel=\"nofollow\">NCT06873334<\/a>)\ub294 \ud638\uc8fc\uc640 \ub274\uc9c8\ub79c\ub4dc \ub0b4 12\uac1c \uc2dc\ud5d8\uae30\uad00\uc758 2\ub2e8\uacc4 \ubc0f \ucd08\uae30 3\ub2e8\uacc4 \ud5cc\ud305\ud134\ubcd1 \ud658\uc790 120\uba85\uacfc \uc804 \uc138\uacc4 40\uac1c \uc774\uc0c1 \uc2dc\ud5d8\uae30\uad00\uc758 \ub3d9\uc77c \ub2e8\uacc4 \ud658\uc790 400\uba85\uc744 \ub300\uc0c1\uc73c\ub85c SKY-0515\uc758 \uc57d\ub825\ud559, \uc548\uc804\uc131 \ubc0f \uc720\ud6a8\uc131\uc744 \ud3c9\uac00\ud558\uae30 \uc704\ud55c \uc81c2\/3\uc0c1, \ubb34\uc791\uc704\ubc30\uc815, \uc774\uc911\ub208\uac00\ub9bc, \uc704\uc57d \ub300\uc870, \uc6a9\ub7c9 \ubc94\uc704 \uc2dc\ud5d8\uc774\ub2e4. \uc801\ud569\ud55c \ud658\uc790\ub294 \ucd5c\uc18c 12\uac1c\uc6d4\uc758 \ud22c\uc5ec \uae30\uac04 \ub3d9\uc548 \uc138 \uac00\uc9c0 \uc6a9\ub7c9 \uc218\uc900 \uc911 \ud558\ub098\uc758 SKY-0515 \ub610\ub294 \uc704\uc57d\uc744 1\uc77c 1\ud68c \uacbd\uad6c \ud22c\uc5ec \ubc1b\ub294\ub2e4. \ubcf8 \uc2dc\ud5d8\uc740 \ud5cc\ud305\ud134\ubcd1 \ubcd1\ub9ac\ud559\uacfc \uad00\ub828\ub41c RNA \uc2a4\ud50c\ub77c\uc774\uc2f1\uc744 \uc870\uc808\ud558\uace0 mHTT \ubc0f PMS1 \ub2e8\ubc31\uc9c8\uc744 \uac10\uc18c\uc2dc\ud0a4\ub294 SKY-0515\uc758 \uc7a0\uc7ac\ub825\uc744 \ud3c9\uac00\ud558\ub294 \uac83\uc744 \ubaa9\ud45c\ub85c \ud55c\ub2e4. \ucc38\uc5ec \uae30\uad00 \ubc0f \uc801\ud569\uc131 \uae30\uc900\uc744 \ud3ec\ud568\ud55c FALCON-HD\uc5d0 \ub300\ud55c \ucd94\uac00 \uc815\ubcf4\ub294 <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=3392531158&amp;u=http%3A%2F%2Fclinicaltrials.gov%2F&amp;a=ClinicalTrials.gov\" target=\"_blank\" rel=\"nofollow\">ClinicalTrials.gov<\/a> \ubc0f <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=2940615165&amp;u=http%3A%2F%2Fwww.falcon-hd.com%2F&amp;a=www.FALCON-HD.com\" target=\"_blank\" rel=\"nofollow\">www.FALCON-HD.com<\/a>\uc5d0\uc11c \ud655\uc778\ud560 \uc218 \uc788\ub2e4.<\/p>\n<p><b>\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4 \uc18c\uac1c<\/b><\/p>\n<p>\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4\ub294 \ub3c5\uc790\uc801\uc778 \ud50c\ub7ab\ud3fc\uc778 SKYSTAR\u00ae\ub97c \uc0ac\uc6a9\ud574 \uc138\uacc4\uc5d0\uc11c \uac00\uc7a5 \ub2e4\ub8e8\uae30 \ud798\ub4e0 \uc9c8\ubcd1\uc744 \uc704\ud55c \uc800\ubd84\uc790 RNA \uc870\uc808 \uce58\ub8cc\uc81c\ub97c \ubc1c\uacac\ud558\uace0 \uac1c\ubc1c\ud558\ub294 \uc784\uc0c1 \ub2e8\uacc4 \ubc14\uc774\uc624\ud14c\ud06c \uae30\uc5c5\uc774\ub2e4. \uc790\uc138\ud55c \uc815\ubcf4\ub294 <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=2221910772&amp;u=http%3A%2F%2Fwww.skyhawktx.com%2F&amp;a=www.skyhawktx.com\" target=\"_blank\" rel=\"nofollow\">www.skyhawktx.com<\/a>\uc5d0\uc11c \ud655\uc778\ud560 \uc218 \uc788\ub2e4.<\/p>\n<p><b>\uc2a4\uce74\uc774\ud638\ud06c \ubb38\uc758\ucc98<br \/><\/b>\ubaa8\ub77c \ub9e4\uce74\uc2dc(Maura McCarthy)<br \/>\uae30\uc5c5 \uac1c\ubc1c \ucd1d\uad04<br \/><a href=\"mailto:maura@skyhawktx.com\" target=\"_blank\" rel=\"nofollow\">maura@skyhawktx.com<\/a><\/p>\n<p>\uc0ac\uc9c4 &#8211; <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=810804790&amp;u=https%3A%2F%2Fmma.prnewswire.com%2Fmedia%2F2870056%2FSkyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg&amp;a=https%3A%2F%2Fmma.prnewswire.com%2Fmedia%2F2870056%2FSkyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg\" target=\"_blank\" rel=\"nofollow\">http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/01\/Skyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg<\/a><\/p>\n<p>\ub85c\uace0 &#8211; <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=2056359031&amp;u=https%3A%2F%2Fmma.prnewswire.com%2Fmedia%2F710814%2FSkyhawk_Therapeutics_Logo.jpg&amp;a=https%3A%2F%2Fmma.prnewswire.com%2Fmedia%2F710814%2FSkyhawk_Therapeutics_Logo.jpg\" target=\"_blank\" rel=\"nofollow\">http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/01\/Skyhawk_Therapeutics_Logo.jpg<\/a><\/p>","protected":false},"excerpt":{"rendered":"<p><!-- wp:html --><\/p>\n<p><img decoding=\"async\" src=\"https:\/\/mma.prnasia.com\/media2\/2870056\/Skyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg?p=medium600\" title=\"\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4, \ud5cc\ud305\ud134\ubcd1 \uce58\ub8cc\uc81c SKY-0515 \uc81c1\uc0c1 \uc784\uc0c1\uc2dc\ud5d8 \ud658\uc790 \ub300\uc0c1 9\uac1c\uc6d4 \uc911\uac04 \uacb0\uacfc \ubc1c\ud45c\" \/><\/p>\n<table border=\"0\" cellspacing=\"10\" cellpadding=\"5\" align=\"right\">\n<tbody>\n<tr>\n<td><img decoding=\"async\" src=\"https:\/\/mma.prnasia.com\/media2\/710814\/Skyhawk_Therapeutics_Logo.jpg?p=medium600\" border=\"0\" alt=\"\" title=\"logo\" hspace=\"0\" vspace=\"0\" width=\"118\" \/><\/td>\n<\/tr>\n<\/tbody>\n<\/table>\n<p class=\"prntac\"><i>9\uac1c\uc6d4 \ubd84\uc11d \uacb0\uacfc \ubcf5\ud569 \ud1b5\ud569 \ud5cc\ud305\ud134\ubcd1 \ub4f1\uae09 \ucc99\ub3c4\uac00 \uae30\uc800\uce58 \ub300\ube44 \ud3c9\uade0 0.64\uc810 \uac1c\uc120-\uc131\ud5a5 \uc810\uc218 \uac00\uc911\uce58 \uc801\uc6a9 \uc2dc \uc99d\uc0c1 \ubc1c\ud604 \ud658\uc790\uc758 9\uac1c\uc6d4 \uc608\uc0c1 \uc790\uc5f0 \uacbd\uacfc \uc545\ud654 \uc218\uce58\uc778 -0.73\uc810 \ub300\ube44<\/i><\/p>\n<p class=\"prntac\"><i>\uc2a4\uce74\uc774\ud638\ud06c, SKY-0515\uc758 \uc784\uc0c1 2\/3\uc0c1\uc778 FALCON-HD \uc2dc\ud5d8\uc744 \uc804 \uc138\uacc4\ub85c \ud655\ub300\ud55c\ub2e4\uace0 \ubc1c\ud45c- \ud604\uc7ac\uae4c\uc9c0 90\uba85 \uc774\uc0c1\uc758 \ud658\uc790\uc5d0\uac8c \ud22c\uc57d \uc2dc\ud589<\/i><\/p>\n<p><span class=\"legendSpanClass\">\ubcf4\uc2a4\ud134<\/span>, <span class=\"legendSpanClass\">2026\ub144 1\uc6d4 27\uc77c<\/span> \/PRNewswire\/ &#8212; \uc911\uc694\ud55c RNA \ud45c\uc801\uc744 \uc870\uc808\ud558\ub294 \ud601\uc2e0\uc801 \uc800\ubd84\uc790 \uce58\ub8cc\uc81c\ub97c \uac1c\ubc1c \uc911\uc778 \uc784\uc0c1 \ub2e8\uacc4 \ubc14\uc774\uc624\ud14c\ud06c \uae30\uc5c5 <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=1326970215&amp;u=https%3A%2F%2Fedge.prnewswire.com%2Fc%2Flink%2F%3Ft%3D0%26l%3Den%26o%3D4603860-1%26h%3D3220405556%26u%3Dhttps%253A%252F%252Fwww.skyhawktx.com%252F%26a%3DSkyhawk%2BTherapeutics%252C%2BInc.&amp;a=%EC%8A%A4%EC%B9%B4%EC%9D%B4%ED%98%B8%ED%81%AC+%ED%85%8C%EB%9D%BC%ED%93%A8%ED%8B%B1%EC%8A%A4(Skyhawk+Therapeutics%2C+Inc.)\" target=\"_blank\" rel=\"nofollow\">\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4(Skyhawk Therapeutics, Inc.)<\/a>\uac00 1\uc6d4 27\uc77c \uc790\uc0ac\uc758 \ud5cc\ud305\ud134\ubcd1(Huntington&#8217;s disease, HD) \uc784\uc0c1\uc2dc\ud5d8 \uce58\ub8cc\uc81c\uc778 SKY-0515\uc758 9\uac1c\uc6d4 \uc911\uac04 \ubd84\uc11d\uc5d0\uc11c \uae0d\uc815\uc801\uc778 \uacb0\uacfc\uac00 \ub3c4\ucd9c\ub410\ub2e4\uace0 \ubc1c\ud45c\ud588\ub2e4.<\/p>\n<div dir=\"ltr\">   <a href=\"https:\/\/mma.prnasia.com\/media2\/2870056\/Skyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg?p=medium600\" target=\"_blank\"><img decoding=\"async\" title=\"Skyhawk Therapeutics, Inc.\" src=\"https:\/\/mma.prnasia.com\/media2\/2870056\/Skyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg?p=medium600\" alt=\"Skyhawk Therapeutics, Inc.\" align=\"middle\" \/><\/a>   <br \/>   <span>Skyhawk Therapeutics, Inc.<\/span>  <\/div>\n<p>SKY-0515 \ud22c\uc5ec \uacb0\uacfc 9mg \uc6a9\ub7c9\uc5d0\uc11c \ud608\uc561 \ub0b4 \ubcc0\uc774 \ud5cc\ud305\ud2f4 \ub2e8\ubc31\uc9c8(mHTT)\uc774 62% \uac10\uc18c\ud558\ub294 \ub4f1 \uc6a9\ub7c9 \uc758\uc874\uc801 \uac10\uc18c\uac00 \ub098\ud0c0\ub0ac\uc73c\uba70, \uccb4\uc138\ud3ec CAG \ubc18\ubcf5 \ud655\uc7a5 \ubc0f \ud5cc\ud305\ud134\ubcd1 \ubcd1\ub9ac\ud559\uc758 \ud575\uc2ec \ub3d9\uc778\uc778 PMS1 mRNA\ub294 26% \uac10\uc18c\ud588\ub2e4. \ub610\ud55c SKY-0515\ub294 \uc6b0\uc218\ud55c \uc911\ucd94\uc2e0\uacbd\uacc4 \ub178\ucd9c\uc744 \uc785\uc99d\ud588\uc73c\uba70 \uc804\ubc18\uc801\uc73c\ub85c \uc548\uc804\ud558\uace0 \ub0b4\uc57d\uc131\uc774 \uc6b0\uc218\ud55c \uac83\uc73c\ub85c \ub098\ud0c0\ub0ac\ub2e4.<\/p>\n<p>\uc81c1\uc0c1 \uc784\uc0c1\uc2dc\ud5d8 \ud30c\ud2b8 C \ud658\uc790 \ucf54\ud638\ud2b8\uc5d0\uc11c SKY-0515\ub97c \ud22c\uc5ec\ubc1b\uc740 \ud658\uc790\ub4e4\uc740 3\uac1c\uc6d4, 6\uac1c\uc6d4, 9\uac1c\uc6d4 \ucc28\uc5d0 \uae30\uc800\uce58 \ub300\ube44 \ud3c9\uade0 \ubcf5\ud569 \ud1b5\ud569 \ud5cc\ud305\ud134\ubcd1 \ub4f1\uae09 \ucc99\ub3c4(Composite Unified Huntington&#8217;s Disease Rating Scale, cUHDRS)\uc758 \uac1c\uc120\uc744 \ubcf4\uc600\ub2e4. 9\uac1c\uc6d4 \ucc28 \ud1b5\ud569 \ubd84\uc11d\uc5d0\uc11c \ud655\uc778\ub41c \uac1c\uc120 \uc218\uce58\ub294 +0.64\uc810\uc73c\ub85c, \uc774\ub294 Enroll-HD \ubc0f TRACK-HD\ub97c \ud65c\uc6a9\ud55c \uc131\ud5a5 \uc810\uc218 \uac00\uc911\uce58 \uae30\uc900 \uc99d\uc0c1 \ubc1c\ud604 \ud658\uc790\uc758 9\uac1c\uc6d4 \uc608\uc0c1 \uc545\ud654 \uc218\uce58\uc778 -0.73\uc810\uacfc \ube44\uad50\ub418\ub294 \uc218\uce58\ub2e4.<\/p>\n<p>\uc720\ub2c8\ubc84\uc2dc\ud2f0 \uce7c\ub9ac\uc9c0 \ub7f0\ub358\uc758 \uc5d0\ub4dc \uc640\uc77c\ub4dc(Ed Wild) \uc2e0\uacbd\ud559 \uad50\uc218\ub294 &#8220;\ud658\uc790 \ub300\uc0c1 SKY-0515 \uc784\uc0c1 1\uc0c1 \ud30c\ud2b8 C\uc5d0\uc11c \ud655\uc778\ub41c \uc548\uc804\uc131 \ubc0f \ucd08\uae30 \ud6a8\ub2a5 \ub370\uc774\ud130\uc5d0 \ub9e4\uc6b0 \uace0\ubb34\ub3fc \uc788\uc73c\uba70, \ud2b9\ud788 \uc0ac\uc804 \uc124\uc815\ub41c 3, 6, 9\uac1c\uc6d4 \ubd84\uc11d\uc5d0\uc11c cUHDRS \uc218\uce58\uac00 \uc608\uc0c1\ub418\ub294 \uc790\uc5f0 \uacbd\uacfc\uc801 \uc545\ud654 \uc591\uc0c1\uc5d0\uc11c \ubc97\uc5b4\ub098\ub294 \uac83\uc744 \ud655\uc778\ud588\ub2e4&#8221;\ub77c\uace0 \ubc1d\ud614\ub2e4. \ub610\ud55c &#8220;SKY-0515\ub294 \ud604\uc7ac\uae4c\uc9c0 \ud658\uc790\ub97c \ub300\uc0c1\uc73c\ub85c \ud14c\uc2a4\ud2b8\ub41c \uadf8 \uc5b4\ub5a4 \uce58\ub8cc\uc81c\ubcf4\ub2e4 \ud070 \ud3ed\uc73c\ub85c mHTT \ub2e8\ubc31\uc9c8\uc744 \uc9c0\uc18d\uc801\uc73c\ub85c \uac10\uc18c\uc2dc\ud0a4\uace0 \uc788\uc73c\uba70, \uc784\uc0c1 \ubc0f \uc0dd\uccb4 \ud45c\uc9c0\uc790\uc0dd\uccb4\ud45c\uc9c0\uc790 \ub370\uc774\ud130\ub294 \uc774 \uc57d\ubb3c\uc774 \ud14c\uc2a4\ud2b8\ub41c \ubaa8\ub4e0 \uc6a9\ub7c9\uc5d0\uc11c \ub0b4\uc57d\uc131\uc774 \uc6b0\uc218\ud568\uc744 \ubcf4\uc5ec\uc900\ub2e4. mHTT\uc640 PMS1\uc744 \ubaa8\ub450 \uac10\uc18c\uc2dc\ud0a4\ub294 SKY-0515\uc758 \ub2a5\ub825\uc740 \ub450 \uac00\uc9c0 \ud575\uc2ec \ubcd1\uc6d0\uc131 \uae30\uc804\uc744 \ud1b5\ud574 \ud5cc\ud305\ud134\ubcd1\uc744 \uce58\ub8cc\ud560 \uc218 \uc788\ub294 \uac15\ub825\ud55c \uc870\ud569\uc744 \uc81c\uacf5\ud55c\ub2e4. \ud604\uc7ac \uc9c4\ud589 \uc911\uc778 \uc704\uc57d \ub300\uc870 FALCON-HD \uc2dc\ud5d8\uc5d0\uc11c \uac80\uc99d\ub420 \uc774\ubc88 \uacf5\uac1c \uc2dc\ud5d8 \uacb0\uacfc\ub294 \uc804 \uc138\uacc4 \ud5cc\ud305\ud134\ubcd1 \ud658\uc790\ub4e4\uc5d0\uac8c \uc720\uc758\ubbf8\ud55c \uc601\ud5a5\uc5d0 \ub300\ud55c \uae30\ub300\ub97c \uc2ec\uc5b4\uc8fc\uba70, SKY-0515\uc640 \uac19\uc740 \uacbd\uad6c\uc6a9 \ud5cc\ud305\ud2f4 \uac10\uc18c \uce58\ub8cc\uc81c\ub294 \uc9c4\uc815\uc73c\ub85c \ud601\uc2e0\uc801\uc778 \ubcc0\ud654\ub97c \uac00\uc838\uc62c \uac83\uc774\ub2e4&#8221;\ub77c\uace0 \ub367\ubd99\uc600\ub2e4.<\/p>\n<p>\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4\uc758 \uc138\ub974\uac8c\uc774 \ud30c\uc6b0\uc2dc\ud0a8(Sergey Paushkin) \uc5f0\uad6c\uac1c\ubc1c \ucd1d\uad04\uc740 &#8220;\ub2f9\uc0ac \uc81c1\uc0c1 \uc2dc\ud5d8\uc758 \ubaa9\ud45c\ub294 \uc548\uc804\uc131\uacfc \uc0dd\uccb4 \ud45c\uc9c0\uc790 \ud65c\uc131\uc744 \ud655\ub9bd\ud558\ub294 \uac83\uc774\uc5c8\ub2e4&#8221;\ub77c\uba70 &#8220;9\uac1c\uc6d4 \uc911\uac04 \ub370\uc774\ud130 \ubd84\uc11d\uc5d0\uc11c \ub098\ud0c0\ub09c SKY-0515\uc758 \uac15\ub825\ud55c \uc0dd\uccb4 \ud45c\uc9c0\uc790 \ubc18\uc751\uacfc \uc790\uc5f0\uacbd\uacfc \ub370\uc774\ud130 \ub300\ube44 cUHDRS\uc758 \uac1c\uc120 \uacb0\uacfc\ub294 SKY-0515\uac00 \ud5cc\ud305\ud134\ubcd1\uc5d0 \ub300\ud55c \ubca0\uc2a4\ud2b8 \uc778 \ud074\ub798\uc2a4(best in class) \uc9c8\ud658 \uc870\uc808 \uce58\ub8cc\uc81c\uac00 \ub420 \uc7a0\uc7ac\ub825\uc744 \uac15\uc870\ud55c\ub2e4. \uc774\ubc88 \uc911\uac04 \ub370\uc774\ud130\ub294 SKY-0515\uc758 \uc911\uc694\ud55c \uc774\uc815\ud45c\uc774\uba70, \uc2b9\uc778\ub41c \uc9c8\ud658 \uc870\uc808 \uce58\ub8cc\uc81c\uac00 \uc5c6\ub294 \uce58\uba85\uc801\uc778 \uc9c8\ud658\uc5d0 \ub300\ud574 \uc800\ubd84\uc790 \ud654\ud569\ubb3c \uc2e0\uc57d\ubb3c\uc9c8(first-in-class)\uc744 \uc81c\uacf5\ud558\ub294 \uc2a4\uce74\uc774\ud638\ud06c \ud50c\ub7ab\ud3fc\uc758 \uc704\ub825\uc744 \ubcf4\uc5ec\uc8fc\ub294 \uac83\uc774\ub2e4&#8221;\ub77c\uace0 \ub9d0\ud588\ub2e4.<\/p>\n<p>\ud5cc\ud305\ud134\ubcd1\uc740 \ud76c\uadc0\ud558\uace0 \uc720\uc804\uc801\uc774\uba70 \uacb0\uad6d \uce58\uba85\uc801\uc778 \uacb0\uacfc\ub97c \ucd08\ub798\ud558\ub294 \uc2e0\uacbd\ud1f4\ud589\uc131 \uc9c8\ud658\uc73c\ub85c, \ubbf8\uad6d \ub0b4 4\ub9cc \uba85 \uc774\uc0c1\uc758 \uc99d\uc0c1 \ubc1c\ud604 \ud658\uc790\uac00 \uc788\uc73c\uba70 \uc804 \uc138\uacc4\uc801\uc73c\ub85c \uc218\uc2ed\ub9cc \uba85\uc774 \uc774\ub97c \uc553\uace0 \uc788\ub294 \uac83\uc73c\ub85c \ucd94\uc815\ub41c\ub2e4. \ud604\uc7ac \uc9c8\ubcd1\uc758 \uc9c4\ud589\uc744 \ub2a6\ucd94\uac70\ub098 \uba48\ucd94\ub294 \uc2b9\uc778\ub41c \uce58\ub8cc\uc81c\ub294 \uc5c6\ub2e4. SKY-0515\ub294 \ud68c\uc0ac\uc758 \ud601\uc2e0\uc801\uc778 RNA \uc870\uc808 \ud50c\ub7ab\ud3fc\uc778 SKYSTAR\u00ae\ub97c \ud1b5\ud574 \uac1c\ubc1c\ub41c \uacbd\uad6c\uc6a9 \uc870\uc0ac\uc6a9 \uc800\ubd84\uc790 RNA \uc870\uc808\uc81c\ub2e4. SKY-0515\ub294 HTT \ub2e8\ubc31\uc9c8\uacfc PMS1 \ub2e8\ubc31\uc9c8\uc744 <i>\ubaa8\ub450<\/i> \uce58\ub8cc\uc801\uc73c\ub85c \uac10\uc18c\uc2dc\ud0a8\ub2e4. PMS1\uc740 \uccb4\uc138\ud3ec CAG \ubc18\ubcf5 \ud655\uc7a5 \ubc0f \ud5cc\ud305\ud134\ubcd1 \ubcd1\ub9ac\ud559\uc758 \ub610 \ub2e4\ub978 \ud575\uc2ec \ub3d9\uc778\uc73c\ub85c, \ubcc0\uc774 HTT \uac10\uc18c\uc758 \uc774\uc810\uc744 \ubcf4\uc644\ud560 \uac83\uc73c\ub85c \uae30\ub300\ub41c\ub2e4.<\/p>\n<p>\uc2a4\uce74\uc774\ud638\ud06c\ub294 \ub610\ud55c \ud638\uc8fc\uc640 \ub274\uc9c8\ub79c\ub4dc \ub0b4 12\uac1c \uae30\uad00\uc5d0\uc11c \uc9c4\ud589 \uc911\uc778 SKY-0515 \uc81c 2\/3\uc0c1 FALCON-HD \uc2dc\ud5d8\uc744 \uc804 \uc138\uacc4\ub85c \ud655\ub300\ud588\ub2e4\uace0 \ubc1c\ud45c\ud588\ub2e4. \uc2a4\uce74\uc774\ud638\ud06c\ub294 \ud604\uc7ac\uae4c\uc9c0 90\uba85 \uc774\uc0c1\uc758 \ud658\uc790\uc5d0\uac8c SKY-0515 \ud22c\uc57d\uc744 \uc644\ub8cc\ud588\ub2e4.<\/p>\n<p>SKY-0515\ub294 \uc2a4\uce74\uc774\ud638\ud06c\uac00 \ucc98\uc74c\uc73c\ub85c \uc784\uc0c1 \uc2dc\ud5d8\uc744 \uc9c4\ud589\ud55c \uc57d\ubb3c\uc774\ub2e4.<\/p>\n<p>\uc2a4\uce74\uc774\ud638\ud06c\ub294 2027\ub144 \ub9d0\uae4c\uc9c0 \uc2b9\uc778\ub41c \uc9c8\ud658 \uc870\uc808 \uce58\ub8cc\uc81c\uac00 \uc5c6\ub294 \ud76c\uadc0 \uc2e0\uacbd\uacc4 \uc9c8\ud658 \uce58\ub8cc\ub97c \uc704\ud55c \ucd94\uac00 \uc800\ubd84\uc790 \uc57d\ubb3c\ub4e4\uc744 \uc784\uc0c1 \ub2e8\uacc4\uc5d0 \uc9c4\uc785\uc2dc\ud0ac \uacc4\ud68d\uc774\ub2e4.<\/p>\n<p><b>SKY-0515 \uc81c1\uc0c1 \uc784\uc0c1\uc2dc\ud5d8 \uc18c\uac1c<\/b><\/p>\n<p>SKY-0515 \uc81c1\uc0c1 \uc784\uc0c1\uc2dc\ud5d8\uc740 \uac74\uac15\ud55c \uc9c0\uc6d0\uc790\uc640 \ucd08\uae30 \ub2e8\uacc4 \ud5cc\ud305\ud134\ubcd1 \ud658\uc790\ub97c \ub300\uc0c1\uc73c\ub85c SKY-0515\uc758 \uc548\uc804\uc131, \ub0b4\uc57d\uc131, \uc57d\ub3d9\ud559 \ubc0f \uc57d\ub825\ud559\uc744 \ud3c9\uac00\ud558\uae30 \uc704\ud55c \ucd5c\ucd08\uc758 \uc778\uac04 \ub300\uc0c1 \uc784\uc0c1\uc2dc\ud5d8\uc774\ub2e4. \uc2dc\ud5d8\uc740 \uc138 \ud30c\ud2b8\ub85c \ub098\ub25c\ub2e4. \ud30c\ud2b8 A\uc640 B\ub294 \uac74\uac15\ud55c \uc9c0\uc6d0\uc790\ub97c \ub300\uc0c1\uc73c\ub85c SKY-0515\ub97c \ud3c9\uac00\ud588\ub2e4. \ud30c\ud2b8 C\ub294 \ucd08\uae30 \ub2e8\uacc4 \ud5cc\ud305\ud134\ubcd1 \ud658\uc790(HD-ISS 1, 2\ub2e8\uacc4 \ub610\ub294 \uacbd\ubbf8\ud55c 3\ub2e8\uacc4)\ub97c \ub300\uc0c1\uc73c\ub85c \ub450 \uac00\uc9c0 \uc6a9\ub7c9 \uc218\uc900\uc758 SKY-0515\uc640 \uc704\uc57d\uc744 84\uc77c\uac04 \ud22c\uc5ec\ud558\ub294 \uc774\uc911\ub208\uac00\ub9bc, \uc704\uc57d \ub300\uc870, \ubcd1\ub82c \uc124\uacc4 \uc2dc\ud5d8\uc73c\ub85c, \ubaa8\ub4e0 \ucc38\uac00\uc790\ub294 12\uac1c\uc6d4\uc758 \ud65c\uc131 \ud22c\uc5ec \uc5f0\uc7a5 \uae30\uac04 \ub3d9\uc548 \ub208\uac00\ub9bc \ubc29\uc2dd\uc73c\ub85c \uc800\uc6a9\ub7c9 \ub610\ub294 \uace0\uc6a9\ub7c9\uc758 SKY-0515\ub97c \ud22c\uc5ec\ubc1b\ub294\ub2e4. \uc2dc\ud5d8 \ubaa9\uc801\uc5d0\ub294 \ubcc0\uc774 HTT \ub2e8\ubc31\uc9c8 \ubc0f PMS1 mRNA \ud3c9\uac00\uac00 \ud3ec\ud568\ub41c\ub2e4. SKY-0515 \ud30c\ud2b8 C\uc758 \uccab \ud658\uc790 \ud22c\uc57d\uc740 2025\ub144 1\uc6d4\uc5d0 \uc2dc\uc791\ub410\uc73c\uba70, \ud604\uc7ac \uc81c1C\uc0c1 \ub2e8\uacc4\uc758 \ub4f1\ub85d\uc774 \uc644\ub8cc\ub410\ub2e4.<\/p>\n<p><b>SKY-0515 \uc81c2\/3\uc0c1 FALCON-HD \uc784\uc0c1\uc2dc\ud5d8 \uc18c\uac1c<\/b><\/p>\n<p><b>FALCON-HD<\/b>(<a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=3584404727&amp;u=https%3A%2F%2Fedge.prnewswire.com%2Fc%2Flink%2F%3Ft%3D0%26l%3Den%26o%3D4603860-1%26h%3D1632102172%26u%3Dhttps%253A%252F%252Fc212.net%252Fc%252Flink%252F%253Ft%253D0%2526l%253Den%2526o%253D4450835-1%2526h%253D1917935461%2526u%253Dhttps%25253A%25252F%25252Fclinicaltrials.gov%25252Fstudy%25252FNCT06873334%2526a%253DNCT06873334%26a%3DNCT06873334&amp;a=NCT06873334\" target=\"_blank\" rel=\"nofollow\">NCT06873334<\/a>)\ub294 \ud638\uc8fc\uc640 \ub274\uc9c8\ub79c\ub4dc \ub0b4 12\uac1c \uc2dc\ud5d8\uae30\uad00\uc758 2\ub2e8\uacc4 \ubc0f \ucd08\uae30 3\ub2e8\uacc4 \ud5cc\ud305\ud134\ubcd1 \ud658\uc790 120\uba85\uacfc \uc804 \uc138\uacc4 40\uac1c \uc774\uc0c1 \uc2dc\ud5d8\uae30\uad00\uc758 \ub3d9\uc77c \ub2e8\uacc4 \ud658\uc790 400\uba85\uc744 \ub300\uc0c1\uc73c\ub85c SKY-0515\uc758 \uc57d\ub825\ud559, \uc548\uc804\uc131 \ubc0f \uc720\ud6a8\uc131\uc744 \ud3c9\uac00\ud558\uae30 \uc704\ud55c \uc81c2\/3\uc0c1, \ubb34\uc791\uc704\ubc30\uc815, \uc774\uc911\ub208\uac00\ub9bc, \uc704\uc57d \ub300\uc870, \uc6a9\ub7c9 \ubc94\uc704 \uc2dc\ud5d8\uc774\ub2e4. \uc801\ud569\ud55c \ud658\uc790\ub294 \ucd5c\uc18c 12\uac1c\uc6d4\uc758 \ud22c\uc5ec \uae30\uac04 \ub3d9\uc548 \uc138 \uac00\uc9c0 \uc6a9\ub7c9 \uc218\uc900 \uc911 \ud558\ub098\uc758 SKY-0515 \ub610\ub294 \uc704\uc57d\uc744 1\uc77c 1\ud68c \uacbd\uad6c \ud22c\uc5ec \ubc1b\ub294\ub2e4. \ubcf8 \uc2dc\ud5d8\uc740 \ud5cc\ud305\ud134\ubcd1 \ubcd1\ub9ac\ud559\uacfc \uad00\ub828\ub41c RNA \uc2a4\ud50c\ub77c\uc774\uc2f1\uc744 \uc870\uc808\ud558\uace0 mHTT \ubc0f PMS1 \ub2e8\ubc31\uc9c8\uc744 \uac10\uc18c\uc2dc\ud0a4\ub294 SKY-0515\uc758 \uc7a0\uc7ac\ub825\uc744 \ud3c9\uac00\ud558\ub294 \uac83\uc744 \ubaa9\ud45c\ub85c \ud55c\ub2e4. \ucc38\uc5ec \uae30\uad00 \ubc0f \uc801\ud569\uc131 \uae30\uc900\uc744 \ud3ec\ud568\ud55c FALCON-HD\uc5d0 \ub300\ud55c \ucd94\uac00 \uc815\ubcf4\ub294 <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=3392531158&amp;u=http%3A%2F%2Fclinicaltrials.gov%2F&amp;a=ClinicalTrials.gov\" target=\"_blank\" rel=\"nofollow\">ClinicalTrials.gov<\/a> \ubc0f <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=2940615165&amp;u=http%3A%2F%2Fwww.falcon-hd.com%2F&amp;a=www.FALCON-HD.com\" target=\"_blank\" rel=\"nofollow\">www.FALCON-HD.com<\/a>\uc5d0\uc11c \ud655\uc778\ud560 \uc218 \uc788\ub2e4.<\/p>\n<p><b>\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4 \uc18c\uac1c<\/b><\/p>\n<p>\uc2a4\uce74\uc774\ud638\ud06c \ud14c\ub77c\ud4e8\ud2f1\uc2a4\ub294 \ub3c5\uc790\uc801\uc778 \ud50c\ub7ab\ud3fc\uc778 SKYSTAR\u00ae\ub97c \uc0ac\uc6a9\ud574 \uc138\uacc4\uc5d0\uc11c \uac00\uc7a5 \ub2e4\ub8e8\uae30 \ud798\ub4e0 \uc9c8\ubcd1\uc744 \uc704\ud55c \uc800\ubd84\uc790 RNA \uc870\uc808 \uce58\ub8cc\uc81c\ub97c \ubc1c\uacac\ud558\uace0 \uac1c\ubc1c\ud558\ub294 \uc784\uc0c1 \ub2e8\uacc4 \ubc14\uc774\uc624\ud14c\ud06c \uae30\uc5c5\uc774\ub2e4. \uc790\uc138\ud55c \uc815\ubcf4\ub294 <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=2221910772&amp;u=http%3A%2F%2Fwww.skyhawktx.com%2F&amp;a=www.skyhawktx.com\" target=\"_blank\" rel=\"nofollow\">www.skyhawktx.com<\/a>\uc5d0\uc11c \ud655\uc778\ud560 \uc218 \uc788\ub2e4.<\/p>\n<p><b>\uc2a4\uce74\uc774\ud638\ud06c \ubb38\uc758\ucc98<br \/><\/b>\ubaa8\ub77c \ub9e4\uce74\uc2dc(Maura McCarthy)<br \/>\uae30\uc5c5 \uac1c\ubc1c \ucd1d\uad04<br \/><a href=\"mailto:maura@skyhawktx.com\" target=\"_blank\" rel=\"nofollow\">maura@skyhawktx.com<\/a><\/p>\n<p>\uc0ac\uc9c4 &#8211; <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=810804790&amp;u=https%3A%2F%2Fmma.prnewswire.com%2Fmedia%2F2870056%2FSkyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg&amp;a=https%3A%2F%2Fmma.prnewswire.com%2Fmedia%2F2870056%2FSkyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg\" target=\"_blank\" rel=\"nofollow\">https:\/\/mma.prnasia.com\/media2\/2870056\/Skyhawk_Therapeutics_9_MONTH_DATA_Graph.jpg?p=medium600<\/a><\/p>\n<p>\ub85c\uace0 &#8211; <a href=\"https:\/\/edge.prnewswire.com\/c\/link\/?t=0&amp;l=ko&amp;o=4603860-1&amp;h=2056359031&amp;u=https%3A%2F%2Fmma.prnewswire.com%2Fmedia%2F710814%2FSkyhawk_Therapeutics_Logo.jpg&amp;a=https%3A%2F%2Fmma.prnewswire.com%2Fmedia%2F710814%2FSkyhawk_Therapeutics_Logo.jpg\" target=\"_blank\" rel=\"nofollow\">https:\/\/mma.prnasia.com\/media2\/710814\/Skyhawk_Therapeutics_Logo.jpg?p=medium600<\/a><\/p>\n<p><!-- \/wp:html --><\/p>","protected":false},"author":1,"featured_media":28274,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[28],"tags":[],"class_list":["post-26559","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-pr"],"blog_post_layout_featured_media_urls":{"thumbnail":["http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/08\/\uc2a4\uce74\uc774\ud638\ud06c_26559_fca48-150x150.jpg",150,150,true],"full":["http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/08\/\uc2a4\uce74\uc774\ud638\ud06c_26559_fca48.jpg",599,424,false]},"categories_names":{"28":{"name":"PR Newswire","link":"http:\/\/mhjn.dothome.co.kr\/en\/category\/pr%eb%89%b4%ec%8a%a4%ec%99%80%ec%9d%b4%ec%96%b4\/"}},"tags_names":[],"comments_number":"0","wpmagazine_modules_lite_featured_media_urls":{"thumbnail":["http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/08\/\uc2a4\uce74\uc774\ud638\ud06c_26559_fca48-150x150.jpg",150,150,true],"cvmm-medium":["http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/08\/\uc2a4\uce74\uc774\ud638\ud06c_26559_fca48.jpg",300,212,false],"cvmm-medium-plus":["http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/08\/\uc2a4\uce74\uc774\ud638\ud06c_26559_fca48.jpg",292,207,false],"cvmm-portrait":["http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/08\/\uc2a4\uce74\uc774\ud638\ud06c_26559_fca48.jpg",400,283,false],"cvmm-medium-square":["http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/08\/\uc2a4\uce74\uc774\ud638\ud06c_26559_fca48.jpg",599,424,false],"cvmm-large":["http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/08\/\uc2a4\uce74\uc774\ud638\ud06c_26559_fca48.jpg",599,424,false],"cvmm-small":["http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/08\/\uc2a4\uce74\uc774\ud638\ud06c_26559_fca48.jpg",130,92,false],"full":["http:\/\/mhjn.dothome.co.kr\/wp-content\/uploads\/2026\/08\/\uc2a4\uce74\uc774\ud638\ud06c_26559_fca48.jpg",599,424,false]},"_links":{"self":[{"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/posts\/26559","targetHints":{"allow":["GET"]}}],"collection":[{"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/comments?post=26559"}],"version-history":[{"count":2,"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/posts\/26559\/revisions"}],"predecessor-version":[{"id":28277,"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/posts\/26559\/revisions\/28277"}],"wp:featuredmedia":[{"embeddable":true,"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/media\/28274"}],"wp:attachment":[{"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/media?parent=26559"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/categories?post=26559"},{"taxonomy":"post_tag","embeddable":true,"href":"http:\/\/mhjn.dothome.co.kr\/en\/wp-json\/wp\/v2\/tags?post=26559"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}